Speakers

Take a look at our speakers scheduled for this event

Jennifer Avelar

Neurology and Neuromuscular Care Center Neurology Rare Disease Center

Mark Awadalla

Chief Development Officer
Capricor Therapeutics, Inc.

Jonathan Blaize

Director, Field Medical Lead
PTC Therapeutics

Barry Byrne

University of Florida, Gainesville

Jessica Campbell

Diana Castro, MD

Founder and Director
Neurology and Neuromuscular Care Center Neurology Rare Disease Center

Jay Chauhan

Sr. Medical Science Liaison
ITF Therapeutics

Stephen Chrzanowski

Assistant Professor
UMass Chan Medical School

Christine Clemson

SVP, Global Head of Medical Affairs
Entrada Therapeutics

Joanne Donovan

Chief Medical Officer
Edgewise Therapeutics

Ken Ecker

Global Medical Lead New Assets
Grünenthal GmbH

Peter Eimon

Director of Research
Tevard Biosciences

Paul Esteso

Assistant Professor of Pediatrics
Children's Hospital Boston

Matt Fisher

Associate Medical Director, Clinical Science
BioMarin Pharmaceutical

Annie Ganot

Co-founder, SVP Patient Advocacy
Solid Biosciences

Tiffany Garcia

Doctor of Clinical Nutrition

Beth Henriksen

Senior Director Patient Advocacy
Avidity Biosciences, A Novartis Company

Lorna Hill

Medical Affairs Leader
Wave Life Sciences

Cassandra Kaufhold

Medical Science Liaison
NS Pharma

Michael Kelly

Chief Scientific Officer
CureDuchenne

Allan Lara

Assistant Professor
Dell Medical School / University of Texas / Dell Children's Medical Center

Doug Levine, PT

CureDuchenne Certified Physical Therapist
CureDuchenne

Jordan Lynch

Director of Community Engagement
CureDuchenne

Jake Marrazzo

Adult with Duchenne/Advocate
CureDuchenne

Sheryl Marrazzo

Duchenne Mom/Community Engagement
CureDuchenne

Oscar Mayer

Professor of Clinical Pediatrics
Children’s Hospital of Philadelphia

Debra & Paul Miller

Founder
CureDuchenne

Hawken Miller

Advocate
Permobil

Migvis Monduy

Medical Director
Nicklaus Children’s Hospital

Lianna Orlando

VP of Research
CureDuchenne

Gary Owens

Senior Director / Program Lead
Precision BioSciences

Guilherme Panhota

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Tim Revell

Kayla Richards

Pediatric Social Worker
UT Health Austin / Dell Children’s
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Lina Saadat

Director, MSL
Dyne Therapeutics

Rosalia Sandoval

Duchenne Mom/Community Engagement
CureDuchenne

Kelsey Saxon

Community Engagement Coordinator
CureDuchenne

Alka Shaunik

Senior Vice President, Medical Affairs
Catalyst Pharmaceuticals
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Teji Singh

Secretome

Mark Stahl

Executive Director, Clinical Development
Insmed Incorporated

Trina Stelly

Koji Takahashi

Head of Medical Affairs
Regenxbio
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Natalie Truba

Nationwide Children's Hospital

Aravindhan Veerapandiyan

Director
Arkansas Children’s Hospital

Jennifer Wallace

Director, Professional Development
CureDuchenne

David Weber

Medical Director
Children’s Hospital of Philadelphia

Brenda Wong

Chief Medical Advisor
CureDuchenne

More speakers to be added soon!